209 - How A Mom Launched The First Drug Approval in FA

In this Episode:

• You Got This, Mental Health - Feeling seen and heard. Some of the responsibilty is on you.
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• Can a single person make a difference? The amazing story of the first approved drug for Friedreich's ataxia (FA)
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• Thank you notes - Reata Pharmmaceuticals, and Kyle's landlord at work.

As the story goes, in an effort to do whatever she could for her son who lives with Friedreich's ataxia (FA), a concerned mother connected a few important dots about science and the pharmaceutical industry. When she decided to make a phone call to the Friedreich's Ataxia Research Alliance (FARA), she started a series of actions and events that eventually led to the approval of the first treatment for FA, SKYCLARYS. Listen for the details.

Links and Resources:

• Announcement: First Medication to Treat Friedreich's Ataxia Approved on Rare Disease Day!